Gene Therapy— Companies & Signals
Gene therapy represents a revolutionary approach to treating diseases by modifying a patient's genes to correct underlying genetic defects or introduce therapeutic proteins. This innovative field holds significant potential for addressing a wide range of previously untreatable or poorly managed conditions, offering the prospect of one-time curative treatments and substantial long-term value creation. 77 public companies above the $50M floor. Last 90 days: 38 red 8-Ks, 0 insider cluster-buys, 7 running hot in the press.
77
Companies
38
Red 8-Ks · 90d
0
Insider clusters
7
🔥 Media-hot
Companies in Gene Therapy
Refine in search →| # | Ticker | Company | Sector | Mkt cap | 1D | 5D | Volume | Heat | Signals |
|---|---|---|---|---|---|---|---|---|---|
| 1 | BNTC | Benitec Biopharma Inc. | Healthcare | $384.1M | +2.7% | +3.3% | 98K | — | red 8-K |
| 2 | MGTX | MeiraGTx Holdings plc | Healthcare | $888.1M | +3.5% | +9.2% | 683K | — | |
| 3 | VYGR | Voyager Therapeutics, Inc. | Healthcare | $211.5M | -0.3% | -3.8% | 657K | — | red 8-K |
| 4 | NGNE | Neurogene Inc. | Healthcare | $459.8M | +0.8% | +0.1% | 545K | — | red 8-K |
| 5 | MXCT | MAXCYTE, INC. | Healthcare | $120.0M | 0.0% | +5.1% | 1.2M | — | red 8-K |
| 6 | ABEO | ABEONA THERAPEUTICS INC. | Healthcare | $315.2M | +0.9% | -1.6% | 1.3M | — | red 8-K |
| 7 | EDIT | Editas Medicine, Inc. | Healthcare | $383.7M | +12.3% | +14.3% | 3.0M | — | red 8-K |
| 8 | WAT | WATERS CORP /DE/ | Healthcare | $34.9B | -1.5% | +3.0% | 981K | ⚡ | |
| 9 | RVTY | REVVITY, INC. | Healthcare | $11.1B | -1.6% | +12.3% | 2.0M | 🔥 | |
| 10 | IRD | Opus Genetics, Inc. | Healthcare | $333.6M | +1.5% | -0.5% | 824K | — | red 8-K |
| 11 | EWTX | Edgewise Therapeutics, Inc. | Healthcare | $3.7B | -1.3% | +12.1% | 1.9M | ⚡ | |
| 12 | DTIL | PRECISION BIOSCIENCES INC | Healthcare | $157.4M | +8.6% | +11.9% | 775K | — | red 8-K |
| 13 | PRME | Prime Medicine, Inc. | Healthcare | $501.2M | +8.4% | +10.4% | 5.3M | — | red 8-K |
| 14 | WVE | Wave Life Sciences Ltd. | Healthcare | $1.1B | -2.6% | -7.9% | 2.7M | — | |
| 15 | QURE | uniQure N.V. | Healthcare | $1.7B | -0.3% | +6.8% | 2.3M | 🔥 | red 8-K |
| 16 | CRSP | CRISPR Therapeutics AG | Healthcare | $4.9B | +2.6% | +3.7% | 1.8M | ⚡ | red 8-K |
| 17 | SRPT | Sarepta Therapeutics, Inc. | Healthcare | $1.6B | +1.0% | -3.6% | 3.8M | — | red 8-K |
| 18 | PGEN | PRECIGEN, INC. | Healthcare | $1.6B | +1.0% | +10.0% | 6.3M | — | red 8-K |
| 19 | CADL | Candel Therapeutics, Inc. | Healthcare | $627.2M | +5.8% | +13.2% | 1.5M | — | red 8-K |
| 20 | RGNX | REGENXBIO Inc. | Healthcare | $344.3M | +12.9% | +30.4% | 2.5M | ⚡ | |
| 21 | FATE | FATE THERAPEUTICS INC | Healthcare | $240.1M | +15.2% | +12.6% | 5.9M | — | red 8-K |
| 22 | ALLO | Allogene Therapeutics, Inc. | Healthcare | $655.8M | +4.2% | +5.7% | 14.7M | — | red 8-K |
| 23 | PCRX | Pacira BioSciences, Inc. | Healthcare | $904.6M | -0.6% | +10.5% | 392K | — | red 8-K |
| 24 | AUTL | Autolus Therapeutics plc | Healthcare | $415.2M | +2.5% | +10.7% | 960K | — | red 8-K |
| 25 | RARE | Ultragenyx Pharmaceutical Inc. | Healthcare | $2.4B | -0.3% | +5.7% | 4.0M | — | red 8-K |
| 26 | AZTA | Azenta, Inc. | Industrials | $1.0B | +0.0% | +14.6% | 514K | — | red 8-K |
| 27 | OCGN | Ocugen, Inc. | Healthcare | $409.6M | +11.3% | +29.5% | 14.2M | 🔥 | red 8-K |
| 28 | PMN | ProMIS Neurosciences Inc. | Healthcare | $92.8M | +2.1% | +0.7% | 19K | — | red 8-K |
| 29 | KROS | Keros Therapeutics, Inc. | Healthcare | $200.9M | -0.6% | -0.5% | 353K | — | red 8-K |
| 30 | CRL | CHARLES RIVER LABORATORIES INTERNATIONAL, INC. | Healthcare | $9.0B | +4.5% | +24.2% | 1.1M | 🔥 | red 8-K |
| 31 | INSM | INSMED Inc | Healthcare | $21.2B | +1.3% | +6.2% | 2.7M | — | |
| 32 | LYEL | Lyell Immunopharma, Inc. | Healthcare | $315.0M | +9.8% | +6.5% | 200K | — | |
| 33 | NKTX | Nkarta, Inc. | Healthcare | $204.6M | +0.7% | +2.1% | 577K | — | |
| 34 | CRBU | Caribou Biosciences, Inc. | Healthcare | $158.2M | +5.4% | +7.9% | 2.8M | — | |
| 35 | KRYS | Krystal Biotech, Inc. | Healthcare | $9.4B | +1.6% | +10.1% | 287K | ⚡ | |
| 36 | NTLA | Intellia Therapeutics, Inc. | Healthcare | $1.7B | -0.4% | +5.5% | 5.6M | ⚡ | |
| 37 | TTRX | Turn Therapeutics Inc. | Healthcare | $180.1M | -0.3% | +19.8% | 29K | — | |
| 38 | AZN | ASTRAZENECA PLC | Healthcare | $277.2B | +1.4% | +8.2% | 1.6M | 🔥 | |
| 39 | DCI | DONALDSON Co INC | Industrials | $10.0B | -0.1% | +2.9% | 758K | — | |
| 40 | MRK | Merck & Co., Inc. | Healthcare | $294.0B | +0.6% | +12.0% | 9.6M | ⚡ | |
| 41 | IONS | IONIS PHARMACEUTICALS INC | Healthcare | $12.1B | -0.6% | +6.3% | 2.8M | — | red 8-K |
| 42 | TRDA | Entrada Therapeutics, Inc. | Healthcare | $250.8M | -0.4% | +9.1% | 240K | — | red 8-K |
| 43 | PLX | Protalix BioTherapeutics, Inc. | Healthcare | $168.4M | +2.2% | +8.8% | 541K | — | |
| 44 | RNAC | Cartesian Therapeutics, Inc. | Healthcare | $279.4M | +2.3% | -3.1% | 192K | — | red 8-K |
| 45 | MOLN | MOLECULAR PARTNERS AG | Healthcare | $154.2M | +4.2% | +0.3% | 9K | — | |
| 46 | KZIA | KAZIA THERAPEUTICS LTD | Healthcare | $163.2M | +1.7% | +3.3% | 195K | — | |
| 47 | ANVS | Annovis Bio, Inc. | Healthcare | $75.7M | +8.1% | +5.1% | 893K | — | |
| 48 | PLYX | Polaryx Therapeutics, Inc. | Healthcare | $118.1M | +5.4% | +5.0% | 337K | — | |
| 49 | GLW | CORNING INC /NY | Materials | $154.2B | +15.7% | +21.9% | 24.3M | 🔥 | |
| 50 | PRQR | ProQR Therapeutics N.V. | Healthcare | $151.7M | +19.6% | -2.7% | 2.6M | — | |
| 51 | SRRK | Scholar Rock Holding Corp | Healthcare | $5.3B | +0.4% | +11.7% | 2.1M | — | |
| 52 | CDXS | CODEXIS, INC. | Materials | $218.2M | -2.5% | -1.7% | 757K | — | red 8-K |
| 53 | CLLS | Cellectis S.A. | Healthcare | $310.9M | +3.9% | +4.3% | 22K | — | |
| 54 | CYRX | Cryoport, Inc. | Healthcare | $736.9M | +1.8% | +10.2% | 965K | — | |
| 55 | AGIO | AGIOS PHARMACEUTICALS, INC. | Healthcare | $1.8B | +0.4% | +8.4% | 772K | — | red 8-K |
| 56 | REPL | Replimune Group, Inc. | Healthcare | $733.2M | -3.7% | +0.2% | 3.7M | — | |
| 57 | CAPR | CAPRICOR THERAPEUTICS, INC. | Healthcare | $1.5B | -10.0% | -18.9% | 3.2M | — | |
| 58 | A | AGILENT TECHNOLOGIES, INC. | Healthcare | $36.7B | -2.3% | +5.0% | 2.0M | 🔥 | red 8-K |
| 59 | LXEO | Lexeo Therapeutics, Inc. | Healthcare | $343.1M | +1.3% | -4.6% | 1.0M | — | red 8-K |
| 60 | GANX | Gain Therapeutics, Inc. | Healthcare | $71.7M | +13.1% | +7.0% | 12.5M | — |
Membership is matched by keyword from companies’ SEC business descriptions (10-K Item 1) — deterministic, not AI inference. May not be exhaustive; not investment advice.